Innovative Methods for Rare Disease Drug Development (Chapman & Hall/CRC Biostatistics Series) - Image 1

£50.99

CRC Press Innovative Methods for Rare Disease Drug Development (Chapman & Hall/CRC Biostatistics Series)

Name: Innovative Methods for Rare Disease Drug Development (Chapman & Hall/CRC Biostatistics Series)
Brand: CRC Press
Price: 50.99 GBP
Availability: InStock

Education

This is the most expensive it has ever been. Walk away.

£51 today · previous high £51 · all-time low £48

NEW HERE?

Amazon shows you one price. We show you all of them.

Tosheroon watches Amazon prices so you don't have to. Every product on Amazon has a price history — we make it visible. Set the price you'd actually pay, and we'll email you the second it gets there. No app, no account, one email.

WHAT'S ON THIS PAGE

↓ Price chart
when this has been cheap or pricey

↓ Forecast
where the price is heading next

↓ Statistics
all-time high & low, recent range

↑ Price alert
name your number, we'll email you

Price History & Forecast

Grey patches = out of stock. Cheaper = lower on the chart. Hover for exact prices.

Last 62 days • 62 data points (No recent data available)

Historical

Generating forecast...

Price Distribution

Price distribution over 62 days • 2 price levels

Days at Price

Current Price

Price Analysis

Most common price: £51 (53 days, 85.5%)

Price range: £48 - £51

Price levels: 2 different prices over 62 days

Description

In the United States, a rare disease is defined by the Orphan Drug Act as a disorder or condition that affects fewer than 200,000 persons. For the approval of "orphan" drug products for rare diseases, the traditional approach of power analysis for sample size calculation is not feasible because there are only limited number of subjects available for clinical trials. In this case, innovative approaches are needed for providing substantial evidence meeting the same standards for statistical assurance as drugs used to treat common conditions. Innovative Methods for Rare Disease Drug Developmentfocuses on biostatistical applications in terms of design and analysis in pharmaceutical research and development from both regulatory and scientific (statistical) perspectives. Key Features: Reviews critical issues (e.g., endpoint/margin selection, sample size requirements, and complex innovative design). Provides better understanding of statistical concepts and methods which may be used in regulatory review and approval. Clarifies controversial statistical issues in regulatory review and approval accurately and reliably. Makes recommendations to evaluate rare diseases regulatory submissions. Proposes innovative study designs and statistical methods for rare diseases drug development, including n-of-1 trial design, adaptive trial design, and master protocols like platform trials. Provides insight regarding current regulatory guidance on rare diseases drug development like gene therapy.

Key Features

Edition Number - 0001. Pages Count - 320. Binding type - Perfect.

Product Specifications

Brand: CRC Press
Format: paperback
ASIN: 0367502909
Category: Books > Subjects > Science, Nature & Maths > Medicine > Education
Domain: Amazon UK
Release Date: 30 May 2022
Listed Since: 03 March 2022

Barcode

No barcode data available

CRC Press Innovative Methods for Rare Disease Drug Development (Chapman & Hall/CRC Biostatistics Series)

This is the most expensive it has ever been. Walk away.

Price History & Forecast

Price Distribution

Price Analysis

Description

Key Features

Product Specifications

Barcode

Similar Products You Might Like

Drug Development for Rare Diseases (Chapman & Hall/CRC Biostatistics Series)

Drug Development & Rare Pediatric Diseases: Issues, Strategic Plan, & Voucher Program Assessment (Pharmacology-research, Safety Testing and Regulation)

Theory of Drug Development: 61 (Chapman & Hall/CRC Biostatistics Series)

Rare Diseases: Challenges and Opportunities for Social Entrepreneurs

Theory of Drug Development (Chapman & Hall/CRC Biostatistics Series)

Statistical Issues in Drug Development (Statistics in Practice)

Multiple Testing Problems in Pharmaceutical Statistics (Chapman & Hall/CRC Biostatistics Series)

Statistics In the Pharmaceutical Industry: 14 (Chapman & Hall/CRC Biostatistics Series)

Innovative Strategies, Statistical Solutions and Simulations for Modern Clinical Trials (Chapman & Hall/CRC Biostatistics Series)

Multiple Testing Problems in Pharmaceutical Statistics: 33 (Chapman & Hall/CRC Biostatistics Series)

Rare Diseases: Integrative PPPM Approach as the Medicine of the Future: 6 (Advances in Predictive, Preventive and Personalised Medicine, 6)

New Drug Development: An Introduction to Clinical Trials: Second Edition

New Drug Development: An Introduction to Clinical Trials: Second Edition

Success Probability Estimation with Applications to Clinical Trials

Statistical Methods in Biomarker and Early Clinical Development

Communicating Rare Diseases and Disorders in the Digital Age (Advances in Medical Technologies and Clinical Practice)

Statistical Applications from Clinical Trials and Personalized Medicine to Finance and Business Analytics

Adaptive Design Theory and Implementation Using SAS and R (Chapman & Hall/CRC Biostatistics Series)

Adaptive Design Theory and Implementation Using SAS and R (Chapman & Hall/CRC Biostatistics Series)

Multiregional Clinical Trials for Simultaneous Global New Drug Development (Chapman & Hall/CRC Biostatistics Series)

Statistical Thinking for Non-Statisticians in Drug Regulation

Statistical Methods in Biomarker and Early Clinical Development

Quantitative Evaluation of Safety in Drug Development: Design, Analysis and Reporting: 67 (Chapman & Hall/CRC Biostatistics Series)

Real-World Evidence in a Patient-Centric Digital Era (Chapman & Hall/CRC Biostatistics Series)